Every life has value
How ‘rare’ is a rare disease? There is no universal or standard definition of rare disease. A disease that occurs infrequently is generally considered a rare disease. There are between 7000 - 8000 rare diseases, but less than 5% have therapies available to treat them1. Many of these diseases are genetic in origin and therefore have to be managed throughout a person’s life.
Globally, we have developed a portfolio of more than 20 medicines to treat various rare diseases in the areas of hematology and inherited metabolic disorders, including serious, life-long illnesses. There is also a growing focus on gene therapy where our dedicated research unit is working on bringing breakthrough therapies for patients.
1. Ministry of Health and family Welfare, National Policy for Rare Disease, 2021. MHFW, India; 2021.